Dear reader, My name is Lianne Bankert. You may have heard of my brother Matthew and sister Kerrin, as well as my parents Ralph and Cathy. We live in Port Colborne, ON. My brother and sister were diagnosed with MPS IIIA, and for that reason, my parents decided to adopt me from China when I [...]
Help us help. Our support and education programs assist those affected in managing the diagnosis and progression of these rare, often devastating, disorders. Funds raised through donations and special events help fund research that provides hope for a brighter future for all children born with lysosomal diseases. Donate to the Annual Fund Click this link to [...]
November 7, 2018 - REGENXBIO announced that the first subject was dosed at the Children's Hospital of Pittsburgh by a medical team led by Dr. Maria Escolar, Associate Professor of Pediatrics, Director of Program for the Study of Neurodevelopment in Rare Disorders at the Children's Hospital of Pittsburgh and primary investigator for the Phase I/II clinical [...]
On October 21st, I participated in the Scotiabank Marathon (and no, I didn’t run the Marathon… I did a measly 5km) alongside my fiancé and a few great friends. This was my first time participating in a fundraiser for the Canadian MPS Society as an adult, and I can say that I have never been more [...]