This Is A Custom Widget

This Sliding Bar can be switched on or off in theme options, and can take any widget you throw at it or even fill it with your custom HTML Code. Its perfect for grabbing the attention of your viewers. Choose between 1, 2, 3 or 4 columns, set the background color, widget divider color, activate transparency, a top border or fully disable it on desktop and mobile.

This Is A Custom Widget

This Sliding Bar can be switched on or off in theme options, and can take any widget you throw at it or even fill it with your custom HTML Code. Its perfect for grabbing the attention of your viewers. Choose between 1, 2, 3 or 4 columns, set the background color, widget divider color, activate transparency, a top border or fully disable it on desktop and mobile.

Monthly Archives: February 2019

//February

My Sister Jessica

Written and presented by Christina Gentle at the 2018 RARE Gala GalaSpeech Hi everyone, thanks for being here tonight. I’m Christina, Jessica Gentle’s sister. If you were at the Gala last year you might remember the great speech she gave about what it’s like to live with MPS 1, which is also known as Hurler Syndrome. [...]

Sanfilippo and How it Affects My Family

Written by Hannah Gilhuis in the spring of 2014. Imagine if you couldn’t express yourself in the way others around you could. That is what it is like for my siblings Rachel and Mathew, who are living with Sanfilippo Syndrome. How this disease works?  Well we all have enzymes in our bodies.  Some are supposed to [...]

Lysogene and Sarepta Therapeutics Announce Dosing of the First Patient in a Gene Therapy for the Treatment of MPS IIIA (Sanfilippo Syndrome Type A)

Lysogene and Sarepta Therapeutics Announce Dosing of the First Patient in AAVance, a Phase 2/3 Clinical Trial Investigating LYS-SAF302, a Gene Therapy for the Treatment of MPS IIIA (Sanfilippo Syndrome Type A) Trial to assess efficacy on neurodevelopmental status of MPS IIIA patients CAMBRIDGE, Mass. and PARIS – Feb. 14, 2019 – Lysogene (FR0013233475 – LYS), a pioneering [...]