News and Events

/News and Events
News and Events 2017-05-29T22:12:20+00:00
604, 2018

Rare – 15th Annual Ignite Hope Fundraising Gala

RARE - 15th Annual Ignite Hope Fundraising Gala What does RARE mean to you..... special? unusual? out of the ordinary? unique? uncommon? ......but it has special meaning for those [...]

603, 2018

ArmaGen Update on Hurler Syndrome Development Program

AGT-181: Investigational Therapy for the Treatment of Patients with Hurler Syndrome AGT-181 is an investigational enzyme replacement therapy designed to treat both the body-related and central nervous system-related symptoms and complications of MPS I. [...]

1309, 2017

2017 National Family Conference Presentations

2017 National Family Conference Presentations: Emil Kakkis, Christine Haller - Overview of Therapeutic Approaches to the Mucopolysaccharidoses Alexey Pshezhetsky - Pathological Cascades in Neuropathic MPS Disorders Outline Alexey Pshezhetsky - Pathological Cascades [...]

709, 2017

BioMarin Presents Interim Data Treatment of MPS IIIB

News Release Issued: Sep 6, 2017 (8:00am PDT) To view this release online and get more information about BioMarin : IR Room visit: http://investors.biomarin.com/2017-09-06-BioMarin-Presents-Interim-Data-of-Phase-1-2-Study-of-BMN-250-for-Treatment-of-Sanfilippo-B-Syndrome-MPS-IIIB-at-13th-International-Congress-of-Inborn-Errors-of-Metabolism-ICIEM-2017 BioMarin Presents Interim Data of Phase [...]

2508, 2017

2017 National Family Conference

On July 21-23, over 120 guests from across Canada joined us at the Canadian MPS Society's 2017 National Family Conference in Montreal! The weekend was filled with valuable resources, educational presentations, [...]