Clinical Trials

Clinical research is medical research that involves people like you. By taking part in clinical research, you help doctors and researchers learn more about disease and improve health care for people in the future.

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Several new treatments for MPS are currently being investigated in clinical trials.

What Are Clinical Trials?

For any type of new medicine to be approved, it first must be proven to be safe and effective. The federal regulators review scientific data gathered when testing a therapy to help decide if the potential benefits of a medicine outweigh the possible risks. These data are accumulated in preclinical and clinical trials. While preclinical research involves testing the treatment of animals, clinical trials evaluate the safety and effectiveness of the treatment in people.

Typically, clinical trials are classified into four progressive phases in the development of a therapy. Find out more at Abeona Therapeutics which has an excellent resource on the four phases of clinical trials .

Why Would I Want To Take Part In a Clinical Trial?

Participating in a clinical trial can advance medical research and help being new treatments and cures to patients faster.

Results from clinical trials provide information about the benefits and risks of a potential treatment, or ways to prevent, manage or detect a disease.

The decision to volunteer for a clinical trial is important and should always be made in consultation with a physician and members of the research team.

Where Can I Find Clinical Trials for MPS Syndromes?

There are several ongoing clinical trials for investigating treatments for MPS.

As clinical trial updates happen frequently, check for the most up to date information on clinical trials that are currently recruiting participants for various MPS types. (A filter can be applied in the listing for recruitment status: Recruiting or Enrolling by Invitation.) Another more user friendly resource which uses as a source is

As there are over 70 trials available we understand the list may, at first, appear daunting. The Canadian MPS Society is here to help with this process. If you would like assistance, please contact or 1-800-667-1846.