Resources for Courageous Parents
Courageous Parents Network is a non-profit organization and educational platform that orients, empowers and accompanies families and providers...
Research Highlights from the 2022 WORLD Symposium:
MPS I (Hurler syndrome) Orchard Therapeutics Announces Interim Data for OTL-203 Showing Positive Clinical Results in Multiple Disease Manifestations...
The Importance of Newborn Screening
Read Gianna’s story and how it changed the course of her life. Newborn screening gave Gianna a head start in her fight against MPS I. Today marks...