Keep up with what’s happening in the MPS community, industry and research.
News from the MPS Community, industry and research
We are planning this for the Fall this year. Watch this space for more details!
This popular event takes place every 2 years. The next one is scheduled for 2023
MPS I (Hurler syndrome) Orchard Therapeutics Announces Interim Data for OTL-203 Showing Positive Clinical Results in Multiple Disease Manifestations...
Read Gianna’s story and how it changed the course of her life. Newborn screening gave Gianna a head start in her fight against MPS I. Today marks...